2nd Rare and Genetic Neurodegenerative Drug Development Summit

The 2nd Rare and Genetic Neurodegenerative Drug Development Summit is dedicated to drug development strategies for rare and genetic neurodegenerative diseases.

Topics

• The neurodegenerative drug development investing landscape
• How to tailor your regulatory drug development approach for swift approvals
• Commonalities Between Rare & Genetic Neurodegenerative for a Holistic Overview of Disease
• The potential of precision neurology
• Biomarkers to Understand Neurodegenerative Diseases
• Rare Sub-Groups in Clinical Trials to Inform Trial Design & Enhance Success
• Disease History & Preclinical Packages
• Disease Modelling & Efficacy Proof to Enhance Preclinical Efforts
• Extrapolating Insights From Genetically Defined Populations to Target Common Pathways in Broader Diseases Populations
• Human Genetics – What it Teaches us About Rare Diseases