Rare Diseases & Orphan Drugs 2019

Topics

• Rare Pediatric Diseases
• Types of Rare Diseases
• Challenges in Rare Diseases Diagnosis
• Genetic Rare Diseases
• Clinical Case Studies on Rare Diseases
• Rare Nutritional and Metabolic Diseases
• Orphan Drugs Development Barriers
• Rare Diseases of Endocrine System
• Orphan Drugs Development & Current Trends
• Rare Diseases in Bloodstream
• Clinical Trials in Rare Diseases
• Patient Concerns on Orphan Drugs
• FDA approval process of Orphan Drugs Products
• Orphan Drug Pricing Reimbursement & Patient Access
• Ethical issues in Funding Orphan Drugs Research & Development